We are here to develop new medicines to deliver a new future for patients and their families by transforming gene regulation in disease.

Above all we are champions for our patients.  Trust, Respect, Compassion and Integrity define who we are.

THIS is why we are here:

  • TENACITY

  • Relentlessly pursuing transformative medicines
     
  • HUMILITY

  • Unwavering commitment to inclusion, openness, and authenticity
     
  • IMPACT

  • Dedicated to a new future for patients and families
     
  • SPIRIT

  • Celebrating teamwork, courageous ideas, and profound results