October 1, 2019
Muscle Xenografts Reproduce Key Molecular Features of Facioscapulohumeral Muscular Dystrophy
Amber L. Mueller, Andrea O'Neill, Takako I. Jones, Anna Llach, Luis Alejandro Rojas, Paraskevi Sakellariou, Guido Stadler, Woodring E. Wright, David Eyerman, Peter L. Jones, Robert J. Bloch
June 20, 2019
Losmapimod Reduces DUX4 Expression Across Genotypes in FSHD Patient-Derived Myotubes
Alejandro Rojas, Erin Valentine, Joseph Maglio, Anthony Accorsi, Alan Robertson, Ning Shen, Angela Cacace, Lucienne Ronco, Owen Wallace. Fulcrum Therapeutics.
June 20, 2019
Phase 1 Clinical Trial of Losmapimod in FSHD
Michelle L. Mellion [1], Lucienne Ronco [1], Drew Thompson [1], Michelle Hage [1], William Tracewell [1], Sander Brooks [2], Emilie van Brummelen [2], Lisa Pagan [2], Umesh Badrising [3], Baziel Van Engelen [4], Geert Jan Groeneveld [2,3], Diego Cadavid [1]
[1] Fulcrum Therapeutics, Cambridge, MA, USA, [2] Centre for Human Drug Research (CHDR), Leiden, NL, [3] Leiden University Medical Centre, Leiden, NL, [4] Radboud University Medical Centre, Nijmegen, NL
June 20, 2019
Diego Cadavid, Michelle Mellion, Owen Wallace, Lucienne Ronco, Drew Thompson, Alejandro Rojas, Michelle Hage, Robert Gould. Fulcrum Therapeutics.
